Publication Topic

Fryzek J, Bylsma LC, Nordyke RJ, Sorensen HT. Rare disease epidemiology: A Danish population-based program. Poster presented at the International Society for Pharmacoepidemiology, Philadelphia, PA, August 2019.

Malone D, Miller B, Dean R, Arjunji R, Jensen IS, Maru B, Dabbous O. 2019. Abstract PRO10: Use of single dose gene-replacement therapy for the treatment of spinal muscular atrophy type 1: A United States payer budget impact analysis. Value in Health 22(Sup2):S336-S337; doi: 10.1016/j.jval.2019.04.1644.

Arjunji R, Dean R, Jensen IS, Miller B, Menier M, Sproule DM, Feltner DE, Droege M, et al. 2019. Abstract PBI10: Type I spinal muscular atrophy patients treated with AVXS-101 have lower use of ventilatory support, hospitalization, and associated costs compared to those treated with nusinersen. Value in Health 22(Sup 2):S48; doi: 10.1016/j.jval.2019.04.093.

Bylsma LC, Fryzek JP, Cetin K, Callaghan F, Bezold C, Mehta B, Wasser JS. 2019. Systematic literature review of treatments used for adult immune thrombocytopenia (ITP) in the second-line setting. Am J Hematol 94(1):118-132; doi: 10.1002/ajh.25301. PMID: 30264861.

Fryzek JP, Bylsma LC, Nordyke RJ, Sorensen HT. Rare disease epidemiology: A Danish population-based program. Poster presented at National Organization for Rare Disorders’ Rare Disease and Orphan Products Breakthrough Summit, Washington, DC, October 2018.

Broome C, Cunningham JM, Mullins M, Jiang X, Bylsma L, Fryzek J, Rosenthal A. Incidence of thromboembolic events is increased in a retrospective analysis of a large cold agglutinin disease (CAD) cohort. Presented at the American Society of Hematology, Atlanta, GA, December 2017.

Soff GA, Ray-Coquard I, Marfil Rivera LJ, Fryzek J, Mullins M, Bylsma LC, Park JK. Literature review of thrombopoietin receptor agonists (TPO-RA) for chemotherapy-induced thrombocytopenia (CIT). Presented at the European Society for Medical Oncology 2017 Congress, Madrid, Spain, September 2017.

Mullins M, Jiang X, Bylsma LC, Fryzek JP, Reichert H, Chen EC, Kummar S, Rosenthal A. 2017. Cold agglutinin disease burden: A longitudinal analysis of anemia, medications, transfusions, and healthcare utilization. Blood Adv 1(13):839-848; doi: 10.1182/bloodadvances.2017004390. PMID: 29296728.

Babik I, Movva N, Lobo MA. Manipulation of arm support changes the movement dynamics of the trunk, and hands in children with arthrogryposis. Poster presentation at the 12th Motor Control Summer School (MCSS-XII); Antiochian Village, Bolivar, PA, May/June 2015.

Babik I, Libassi L, Movva N, Lobo MA. Rehabilitation intervention changing the dynamics of movement in children with arthrogryposis. Poster presentation at the Society for Research in Child Development Biennial Conference, Philadelphia, PA, March 2015.