Publication Topic
Metachromatic leukodystrophy
2022
Pang F, Dean R, Jensen I, Tehard B, Roze S, Olaye A, et al. 2022. The cost-effectiveness of atidarsagene autotemcel for the treatment of metachromatic leukodystrophy in France. Mol Gene Metab 135(2):S93; doi: 10.1016/j.ymgme.2021.11.242.